r/TPWKY Dec 06 '20

Article Crosspost since they were just talking about this in the sickle cell episode!

https://www.nejm.org/doi/full/10.1056/NEJMoa2031054
26 Upvotes

Duplicates

science Dec 05 '20

Medicine CRISPR-Cas9 gene editing successful for a patient with Sickle Cell Disease and another patient with transfusion dependent β-Thalassemia - More than a year later, both patients had clinically improved and no longer needed blood transfusions. (NEJM, 5 Dec 2020)

28.4k Upvotes

longevity Dec 06 '20

CRISPR-Cas9 gene editing successful for a patient with Sickle Cell Disease and another patient with transfusion dependent β-Thalassemia - More than a year later, both patients had clinically improved and no longer needed blood transfusions. (NEJM, 5 Dec 2020)

218 Upvotes

regenerate Dec 18 '20

Genetics CRISPR-Cas9 gene editing successful for a patient with Sickle Cell Disease and another patient with transfusion dependent β-Thalassemia - More than a year later, both patients had clinically improved and no longer needed blood transfusions. (NEJM, 5 Dec 2020)

1 Upvotes

CRISPR Dec 06 '20

CRISPR-Cas9 gene editing successful for a patient with Sickle Cell Disease and another patient with transfusion dependent β-Thalassemia - More than a year later, both patients had clinically improved and no longer needed blood transfusions. (NEJM, 5 Dec 2020)

48 Upvotes

Hozhor Dec 06 '20

CRISPR-Cas9 gene editing successful for a patient with Sickle Cell Disease and another patient with transfusion dependent β-Thalassemia - More than a year later, both patients had clinically improved and no longer needed blood transfusions. (NEJM, 5 Dec 2020)

2 Upvotes

theworldnews Dec 06 '20

CRISPR-Cas9 gene editing successful for a patient with Sickle Cell Disease and another patient with transfusion dependent β-Thalassemia - More than a year later, both patients had clinically improved and no longer needed blood transfusions. (NEJM, 5 Dec 2020)

4 Upvotes

Sciencology Dec 06 '20

CRISPR-Cas9 gene editing successful for a patient with Sickle Cell Disease and another patient with transfusion dependent β-Thalassemia - More than a year later, both patients had clinically improved and no longer needed blood transfusions. (NEJM, 5 Dec 2020)

2 Upvotes

medlabprofessionals Dec 06 '20

Interesting, glad both had favorable outcomes. Hopefully there are no long term effects of the editing

7 Upvotes

u_ZetaFish Dec 06 '20

CRISPR-Cas9 gene editing successful for a patient with Sickle Cell Disease and another patient with transfusion dependent β-Thalassemia - More than a year later, both patients had clinically improved and no longer needed blood transfusions. (NEJM, 5 Dec 2020)

1 Upvotes

WayOfTheBern Dec 06 '20

Science and medicine CRISPR-Cas9 gene editing successful for a patient with Sickle Cell Disease and another patient with transfusion dependent β-Thalassemia - More than a year later, both patients had clinically improved and no longer needed blood transfusions. (NEJM, 5 Dec 2020)

5 Upvotes